Browsing Genetics (Scholarly Publications) by Sponsor "Irish Research Council for Humanities and Social Sciences (IRCHSS)"
Now showing items 1-1 of 1
-
Suppression and Replacement Gene Therapy for Autosomal Dominant Disease in a Murine Model of Dominant Retinitis Pigmentosa
(2011)For dominantly inherited disorders development of gene therapies, targeting the primary genetic lesion has been impeded by mutational heterogeneity. An example is rhodopsin-linked autosomal dominant retinitis pigmentosa ...